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Neuronal Ceroid Lipofuscinosis 2 - 3 Studies Found
Estado | Estudiar |
Completed |
Nombre del estudio: A Phase 1/2 Open-Label Dose-Escalation Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Efficacy of Intracerebroventricular BMN 190 in Patients With Late-Infantile Neuronal Ceroid Lipofuscinosis (CLN2) Disease Condición:
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