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Glycogen Storage Disease Type I - 6 Studies Found

Status Study
Completed Study Name: A Study to Evaluate the Effects of Pharmacological Chaperones in Cells From Patients With Pompe Disease
Condition:
  • Pompe Disease
  • Glycogen Storage Disease Ty
    Date: 2007-08-10
    Interventions: Other: Observation Ex vivo administration of AT2220
Completed Study Name: An Exploratory Study of the Safety and Efficacy of Prophylactic Immunomodulatory Treatment in Myozyme-naive Cross-Reacting Immunologic Material (CRIM[-]) Patients With Infantile-Onset Pompe Disease
Condition:
  • Pompe Disease
  • Glycogen Storage Disease Ty
    Date: 2008-06-17
    Interventions:
    • Biological: Alglucosidase Alfa

Recruiting Study Name: NeoGAA Extension Study
Condition: Glycogen Storage Disease Type II Pompe Disease
Date: 2013-12-04
Interventions: Drug: GZ402666 Pharmaceutical form:lyophilized powder reconstituted for infusion Route of administration
Recruiting Study Name: Pharmacokinetics of Alglucosidase Alfa in Patients With Pompe Disease
Condition:
  • Pompe Disease (Late-Onset)
  • Glycogen Stora
    Date: 2011-08-02
    Interventions: Biological: alglucosidase alfa Intravenous (IV) infusion of 20mg/kg body weight every other week (qow)
RECRUITING Study Name: A Study to Evaluate the Safety, Efficacy, PK, PD and Immunogenicity of Cipaglucosidase Alfa/Miglustat in IOPD Subjects Aged 0 to <18
Condition: Glycogen Storage Disease Type II Infantile Onset
Date: 2024-10-03
Interventions: Sterile lyophilized powder intravenous (IV) infusion
RECRUITING Study Name: Prospective Collection of Biospecimen in Pediatric Patients and Adult Guardians Diagnosed With Glycogen Storage Disease Type 1B (GSD1b)
Condition: Glycogen Storage Disease Type IB
Date: 2024-10-03
Interventions: blood donation