Search for Clinical Trial Results

Hereditary Central Nervous System Demyelinating Diseases - 20 Studies Found
Status | Study |
Recruiting |
Study Name: Aclarubicin for the Treatment of Retinal Vasculopathy With Cerebral Leukodystrophy Condition:
|
Terminated |
Study Name: Natural History Study of Children With Metachromatic Leukodystrophy Condition:
|
Recruiting |
Study Name: Intracerebral Gene Therapy for Children With Early Onset Forms of Metachromatic Leukodystrophy Condition: Metachromatic Leukodystrophy Date: 2013-01-28 Interventions: Genetic: intracerebral administration of AAVrh.10cuARSA |
Active, not recruiting |
Study Name: Gene Therapy for Metachromatic Leukodystrophy Condition: Lysosomal Storage Disease Date: 2012-03-16 Interventions: Genetic: Autologous CD34+ stem cells transduced with ARSA encoding lentiviral vector Autologous hematopo |
Completed |
Study Name: Multicenter Study of HGT-1110 Administered Intrathecally in Children With Metachromatic Leukodystrophy (MLD) Condition: Metachromatic Leukodystrophy (MLD) Date: 2011-12-14 Interventions: Biological: Recombinant human arylsulfatase A 6 patients treated with HGT-1110 EOW by IT injection |
Completed |
Study Name: Long-Term Follow-Up Study of Human Stem Cells Transplanted in Subjects With Connatal Pelizaeus-Merzbacher Disease (PMD) Condition:
Date: 2011-07-06 Interventions: Biological: HuCNS-SC transplant in the lead-in phase Long-term safety follow-up study |