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Leukodystrophy - 34 Studies Found

Status Study
Recruiting Study Name: Newborn Screening for Adrenoleukodystrophy
Condition: Adrenoleukodystrophy
Date: 2016-10-31
Interventions: Procedure: newborns testing for ALD Routine newborn screening dried blood spots sample is used to test i
Withdrawn Study Name: MT2014-14 IT-MSC for Advanced Cerebral Adrenoleukodystrophy (cALD)
Condition: Cerebral Adrenoleukodystrophy
Date: 2015-03-27
Interventions: Biological: Mesenchymal Stem Cells
Suspended Study Name: Effect of Glycerol Trierucate on Clinical Course of Adrenoleukodystrophy
Condition: Adrenoleukodystrophy
Date: 1999-10-18
Interventions:
  • Drug: glyceryl trierucate Glyc
Available Study Name: Expanded Access for Lorenzo's Oil (GTO/GTE) in Adrenoleukodystrophy
Condition: X-linked Adrenoleukodystrophy
Date: 2014-05-05
Interventions: Drug: Lorenzo's Oil Oral use of Lorenzo's oil to lower very long chain fatty acids
Available Study Name: Clinical Study and Gene Mutation Analysis of Adrenoleukodystrophy in Taiwanese Children
Condition: Adrenoleukodystrophy
Date: 2006-01-16
Interventions: Procedure: blood sampling and medical records
Recruiting Study Name: A Phase 2/3 Study of the Efficacy and Safety of Hematopoietic Stem Cells Transduced With Lenti-D Lentiviral Vector for the Treatment of Cerebral Adrenoleukodystrophy (CALD)
Condition: Cerebral Adrenoleukodystrophy (CALD)
Date: 2013-03-22
Interventions: Genetic: Lenti-D Drug Product Lenti-D Drug Product (autologous CD34+ cell-enriched population that conta
Recruiting Study Name: A Pilot Study of Vitamin D in Boys With X-linked Adrenoleukodystrophy
Condition: X-linked Adrenoleukodystrophy
Date: 2015-10-29
Interventions: Dietary Supplement: vitamin D3 Daily oral supplement provided by study investigators
Completed Study Name: The Effect of Bezafibrate on the Level of Very Long Chain Fatty Acids (VLCFA) in X-linked Adrenoleukodystrophy (X-ALD)
Condition:
  • X-linked Adrenoleukodystrophy
  • Adrenomyelo
    Date: 2010-07-13
    Interventions: Drug: Bezafibrate Week 0 to 12: 400 mg once daily 1 tablet. Week 13 to 24: 400 mg once daily 2 tablets.
Withdrawn Study Name: Safety and Pharmacodynamic Study of Sobetirome in X-Linked Adrenoleukodystrophy (X-ALD)
Condition:
  • X-Linked Adrenoleukodystrophy
  • Adrenomyelo
    Date: 2013-02-06
    Interventions: Drug: Sobetirome 50 mcg or 100 mcg once-daily oral O
Terminated Study Name: A Phase III Trial of Lorenzo's Oil in Adrenomyeloneuropathy
Condition:
  • Adrenomyeloneuropathy
  • Adrenoleukodystroph
    Date: 2007-10-16
    Interventions: Drug: Lorenzo's oil 4:1 glyceryl trioleate-glyceryl trierucate (Lorenzo's oil)given orally, daily as app
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