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Mucopolysaccharidoses - 19 Studies Found

Status Study
Recruiting Study Name: Hematopoietic Stem Cell Transplantation for Mucopolysaccharidosis
Condition: Mucopolysaccharidosis
Date: 2010-11-08
Interventions:
  • Drug: Conditioning regimen

Completed Study Name: Natural History Studies of Mucopolysaccharidosis III
Condition:
  • Mucopolysaccharidosis Type IIIA
  • Mucopolys
    Date: 2013-11-26
    Interventions:
    • Procedure: Lumbar puncture
    • Device: Magneti
Recruiting Study Name: A Study of JR-141 in Patients With Mucopolysaccharidosis Type II
Condition: Mucopolysaccharidosis II
Date: 2017-04-10
Interventions: Drug: JR-141 IV infusion (lyophilized powder), 0.01-2.0 mg/kg/week
Completed Study Name: Study of rhASB in Patients With Mucopolysaccharidosis VI
Condition: Mucopolysaccharidosis VI
Date: 2005-02-24
Interventions:
  • Drug: N-acetylgalactosamine 4-sulfatase

Terminated Study Name: Discovering New Biomarkers For Monitoring Disease Progression in Patients With Mucopolysaccharidosis IVA
Condition: Mucopolysaccharidosis Type IVA
Date: 2012-11-21
Completed Study Name: Diagnosis of Mucopolysaccharidosis Disorders in Patients Presenting With Bilateral Hip Disease
Condition:
  • Mucopolysaccharidosis IV A
  • Mucopolysaccha
    Date: 2012-10-12
    Interventions: Other: Enzyme testing Leukocyte activity measurement of Arylsulfatase B and N acetyl galactosamine 6 sul
Completed Study Name: An Open-Label Phase 1/2 Study to Assess the Safety, Efficacy and Dose of Study Drug UX003 Recombinant Human Beta-glucuronidase (rhGUS) Enzyme Replacement Therapy in Patients With MPS 7
Condition: Mucopolysaccharidosis Type 7
Date: 2013-05-08
Interventions: Drug: UX003
Completed Study Name: Phase I/II Study of Retroviral-Mediated Transfer of Iduronate-2-Sulfatase Gene Into Lymphocytes of Patients With Mucopolysaccharidosis II (Mild Hunter Syndrome)
Condition: Mucopolysaccharidosis II
Date: 1999-10-18
Interventions: Genetic: lymphocyte gene therapy
Recruiting Study Name: Effects of Adalimumab in Mucopolysaccharidosis Types I, II and VI
Condition:
  • Mucopolysaccharidosis Type I
  • Mucopolysacc
    Date: 2015-05-05
    Interventions:
    • Drug: Adalimumab Subjects will
Recruiting Study Name: A Treatment Study of Mucopolysaccharidosis Type IIIB
Condition:
  • MPS III B
  • Mucopolysaccharidosis Type IIIB

Date: 2016-02-27
Interventions: Drug: BMN 250 Chimeric fusion of recombinant human alpha-N-acetylglucosaminidase and truncated human ins
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