Search for Clinical Trial Results

Severe Combined Immunodeficiency - 9 Studies Found
Status | Study |
Completed |
Study Name: Stem Cell Gene Therapy to Treat X-Linked Severe Combined Immunodeficiency (XSCID) Condition: Severe Combined Immunodeficiency Date: 2001-12-17 Interventions: Drug: Gene-Transduced Autologous CD34+ Stem Cells |
Active, not recruiting |
Study Name: Gene Therapy for X-linked Severe Combined Immunodeficiency Condition: X-linked Severe Combined Immunodeficiency Date: 2011-06-21 Interventions: Other: Gene transfer Single infusion of autologous CD34+ cells transduced with the self-inactivating (SI |
Recruiting |
Study Name: Gene Transfer for X-Linked Severe Combined Immunodeficiency in Newly Diagnosed Infants Condition: Severe Combined Immunodeficiency Disease, X-linked Date: 2012-01-13 Interventions:
|
Recruiting |
Study Name: Gene Transfer for Severe Combined Immunodeficiency, X-linked (SCID-X1) Using a Self-inactivating (SIN) Gammaretroviral Vector Condition: Severe Combined Immunodeficiency Date: 2010-05-21 Interventions: Biological: Gene transfer Three procedures: 1) Bone marrow harvest from the patient's posterior iliac cr |
Active, not recruiting |
Study Name: Gene Therapy for X-linked Severe Combined Immunodeficiency (SCID-X1) Condition: X-linked Severe Combined Immunodeficiency Date: 2010-07-29 Interventions: Genetic: Single infusion of autologous CD34+ cells transduced with the self-inactivating (SIN) gammaretroviral vector pSRS11.EFS.IL2RG.pre |
Completed |
Study Name: Influences on Female Adolescents' Decisions Regarding Testing for Carrier Status of XSCID Condition: Severe Combined Immunodeficiency Date: 2000-10-04 |
Recruiting |
Study Name: Lentiviral Gene Transfer for Treatment of Children Older Than Two Years of Age With X-Linked Severe Combined Immunodeficiency (XSCID) Condition:
Interventions: |
Recruiting |
Study Name: Evaluation of Patients With Immune Function Abnormalities Condition: Immune System Diseases Date: 2005-08-09 |
COMPLETED |
Study Name: Long Term Follow Up Of Patients Who Have Received Gene Therapy Or Gene Marked Products Condition: Severe Combined Immunodeficiency Date: 2025-02-17 Interventions: Blood draw |